Sunday investigation. Effective therapies could by no means be accessible to sufferers, attributable to unsuitable and too restrictive regulation.
https://www.lepoint.fr/sante/therapies-geniques-le-scandale-reglementaire-des-maladies-rares-11-05-2025-2589298_40.php
Genic therapies: the regulatory scandal of uncommon ailments | EUROtoday
